#Crispr

Intellia Therapeutics said its Crispr-based treatment for hereditary angioedema met its goals in a Phase 3 trial, marking a milestone for gene editing.

Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a functional cure for the deadly blood disorders sickle cell disease and beta thalassemia.

A fresh approach to trialling treatments for rare genetic diseases could make their production an economically viable prospect at last. A fresh approach to trialling treatments for rare genetic diseases could make their production an economically viable…

From SingularityHub: MIT Mined Bacteria for the Next CRISPR—and Found Hundreds of Potential New Tools

Once delivered to cells, the CRISPR-Cas9 gene-editing system (purple and pink) cuts DNA in specific places.